Adult patients with primary mitochondrial disease research hub

An open-label, single-arm extension study to evaluate the long-term safety, tolerability, and efficacy of KL1333 (napazimone) in patients with primary mitochondrial disease

This study looks at a medicine called KL1333 for adults with a condition called primary mitochondrial disease. It mainly checks if the medicine is safe and if it helps over a longer time. It's a follow-up to earlier research, using a new version of the medicine.