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Anemia in subjects with sickle cell disease (SCD) research hub
2 indexed studies · 0 currently recruiting
- authorisedTherapeutic confirmatory (Phase III)
A Phase 3, Double-Blind, Randomized, Placebo-Controlled, Multicenter Study to Evaluate the Effect of Mitapivat on Transfusion Burden in Subjects With Sickle Cell Disease
This clinical trial is testing a new tablet called mitapivat for adults with sickle cell disease. Researchers want to find out if taking mitapivat every day for one year can safely reduce or stop the need for blood transfusions by helping red blood cells stay healthy for longer.
Italy · France · Belgium - authorisedPhase II and Phase III (Integrated)
A Phase 2/3, Double-Blind, Randomized, Placebo-Controlled, Multicenter Study to Evaluate the Efficacy and Safety of Mitapivat in Subjects With Sickle Cell Disease.
This study is testing a new medicine, Mitapivat, for people with sickle cell disease. It aims to see if the medicine can help increase healthy red blood cells and reduce painful crises. Some people will receive the medicine, and others a dummy pill, to compare effects.
Netherlands · Germany · Belgium