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Ataxia Telangiectasia (A-T) research hub
2 indexed studies · 1 currently recruiting
- recruitingTherapeutic confirmatory (Phase III)
An Open-Label Extension Study of EryDex in Patients with Ataxia-Telangiectasia Following Participation in Study IEDAT-04-2022 (NEAT)
This study is an extension of a previous trial, looking at the long-term safety of an experimental medicine called EryDex for people with Ataxia-Telangiectasia (A-T). It checks for any side effects and how the medicine affects important body functions.
Denmark · Norway · Germany - active not recruitingPHASE3
A Pivotal Study of N-Acetyl-L-Leucine on Ataxia-Telangiectasia (A-T)
This study is testing a new medicine, N-Acetyl-L-Leucine, for Ataxia-Telangiectasia (A-T). It aims to see if the medicine is safe, well-tolerated, and effective in improving symptoms, compared to a dummy treatment.
United States · Germany · Slovakia