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Cerebral Adrenoleukodystrophy (CALD) research hub

2 indexed studies · 0 currently recruiting

active not recruiting
Long-term Follow-up of Participants With Cerebral Adrenoleukodystrophy Who Were Treated With Lenti-D Drug Product
This study is following up on children and young men who have a serious brain condition called cerebral adrenoleukodystrophy (CALD). They previously received a special gene therapy called Lenti-D (or eli-cel) in an earlier study. This new study checks on their health over a very long time, up to 15 years.
United States · Argentina · Australia
active not recruitingPHASE3
A Clinical Study to Assess the Efficacy and Safety of Leriglitazone in Adult Male Subjects With Cerebral Adrenoleukodystrophy
This study looks at a new drug called Leriglitazone for adult men with a brain condition called cerebral adrenoleukodystrophy (cALD). Researchers want to see if it's safe and helps improve or slow down the disease.
United States · Argentina · Brazil