Congenital Adrenal Hyperplasia research hub
8 indexed studies · 5 currently recruiting
- recruitingPHASE1, PHASE2
A Trial of Lu AG13909 in Participants With Congenital Adrenal Hyperplasia
This study is looking into a new medicine called Lu AG13909 for adults with Congenital Adrenal Hyperplasia (CAH). It will check if the medicine is safe, how the body handles it, and how effective it is in different doses.
United States · Denmark · France - recruitingPHASE2
An Extension Study to Evaluate Safety and Efficacy in Participants Treated With CRN04894
This study looks at the long-term safety and effectiveness of a new medicine, atumelnant, for people with Congenital Adrenal Hyperplasia (CAH). It's for those who have already tried atumelnant in a previous study and could benefit from continuing it.
United States · Argentina · Brazil - recruitingPHASE3
A Study to Evaluate Atumelnant in Adults With Congenital Adrenal Hyperplasia
This study is testing a new medicine, atumelnant, for adults with a condition called congenital adrenal hyperplasia (CAH). It aims to see if the medicine is safe, works well, and how the body handles it.
United States · Argentina · Australia - recruitingPHASE2, PHASE3
A Study in Pediatric Participants With Congenital Adrenal Hyperplasia (Balance-CAH)
This study is looking into a new medication called atumelnant for children and teenagers with a condition called Congenital Adrenal Hyperplasia (CAH). It wants to see if the medication is safe, works well, and how the body handles it.
United States · Argentina · Australia - active not recruitingPHASE3
Global Safety and Efficacy Registration Study of Crinecerfont in Pediatric Participants With Classic Congenital Adrenal Hyperplasia (CAHtalyst Pediatric Study)
This study is testing a new medicine, crinecerfont, for children and teenagers aged 2 to 17 with a type of Congenital Adrenal Hyperplasia (CAH). It compares the new medicine to a dummy pill (placebo) to see how well it works and if it's safe.
United States · Belgium · Canada - active not recruitingPHASE3
Global Safety and Efficacy Registration Study of Crinecerfont for Congenital Adrenal Hyperplasia
This study is testing a new medicine, crinecerfont, for adults with a condition called Congenital Adrenal Hyperplasia (CAH). It will compare crinecerfont to a dummy medicine to see if it's safe and helps manage CAH over about 20 months.
United States · Austria · Belgium - not yet recruitingNA
Growing up With the Young Endocrine Support System (YESS!)
This study looks at a new game, YESS!, and a toolkit to help young people with long-term hormone conditions manage their health better as they move from children's to adult healthcare. The aim is to help them feel more in control and stick with their doctor's appointments.
Belgium · Netherlands · Spain - ongoing, recruitingTherapeutic exploratory (Phase II)
A 12-Week, Phase 2 Open-Label, Sequential Dose Cohort Study to Evaluate the Safety, Efficacy, and Pharmacokinetics of CRN04894 Treatment in Participants with Congenital Adrenal Hyperplasia
Germany · Italy