- recruiting
Defining Outcome Measures for Behavioural and Emotional Problems in Dystrophinopathies
This study looks at how Duchenne (DMD) and Becker (BMD) muscular dystrophies affect thinking, feelings, and behaviour. It uses computer tasks and questionnaires to understand how the brain responds and to help create better ways to measure these effects in future research.
United Kingdom - recruitingPHASE2
Phase 2 Study of SAT-3247 in Pediatric Ambulatory Patients
This study is testing a new medicine, SAT-3247, for boys aged 7-9 with Duchenne muscular dystrophy. We want to find the best dose, see if it's safe, and check if it helps. Some boys will get the real medicine, others a dummy medicine.
United States · Australia · Belgium