Duchenne Muscular Dystrophy research hub

Phase 2 Study of SAT-3247 in Pediatric Ambulatory Patients

This study is testing a new medicine, SAT-3247, for boys aged 7-9 with Duchenne muscular dystrophy. We want to find the best dose, see if it's safe, and check if it helps. Some boys will get the real medicine, others a dummy medicine.