Research.Patient.info
Facioscapulohumeral Muscular Dystrophy (FSHD) research hub
3 indexed studies · 0 currently recruiting
- active not recruitingPHASE2
A Study to Evaluate RO7204239 in Participants With Facioscapulohumeral Muscular Dystrophy
This study is looking into a new medication called RO7204239 for adults with Facioscapulohumeral Muscular Dystrophy (FSHD). It aims to see how safe and effective the medication is, and how it affects the body.
United States · Denmark · Italy - ongoing, recruitingPhase I and Phase II (Integrated)- First administration to humans
A Randomized, Double-blind, Placebo-controlled, Phase 1/2 Study to Evaluate the Safety, Tolerability, Pharmacokinetics, Pharmacodynamics, and Exploratory Efficacy of AOC 1020 Administered Intravenously to Adult Participants with Facioscapulohumeral Muscular Dystrophy (FSHD)
This study is testing a new medicine, AOC 1020, for people with Facioscapulohumeral Muscular Dystrophy (FSHD). We want to see if it's safe, how the body handles it, and if it helps. This is one of the first times this medicine will be given to people.
Netherlands · Italy - ongoing, recruitingTherapeutic confirmatory (Phase III)
A Phase 3 Global, Randomized, Double-Blind, Placebo-Controlled, 48-Week, Parallel-Group Study of the Efficacy and Safety of Losmapimod in Treating Patients With Facioscapulohumeral Muscular Dystrophy (FSHD) (REACH)
This study is testing a new tablet, losmapimod, for people with Facioscapulohumeral Muscular Dystrophy (FSHD). It aims to see if the drug helps improve arm function and if it's safe to use over time.
Italy · Spain · France