Fanconi Anemia research hub

Long-Term Follow-up: Phase I/II Clinical Study to Evaluate the Safety and Efficacy of the Infusion of RP-L102

This study is checking on people who received a special treatment called RP-L102 for Fanconi Anaemia. It aims to see how safe and effective the treatment is over many years. If you were part of a previous RP-L102 study, you might be able to join this one.