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Hereditary Transthyretin Amyloidosis with Polyneuropathy (ATTRv-PN) research hub

1 indexed studies · 0 currently recruiting

ongoing, recruitingHuman Pharmacology (Phase I)- First administration to humans
Phase 1 Two-Part (Open-label, Single Ascending Dose (Part 1) and Open-label, Single Dose Expansion (Part 2)) Study to Evaluate Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of NTLA-2001 in Patients With Hereditary Transthyretin Amyloidosis With Polyneuropathy (ATTRv-PN).
France · Sweden