Huntington's Disease research hub

Enroll -HD: A Prospective Registry Study in a Global Huntington's Disease Cohort

Enroll-HD is a long-term study collecting information and samples from people with or at risk of Huntington's disease (HD), and their families. This helps researchers worldwide better understand HD, find new ways to treat it, and design better clinical trials for the future.

A Study to Evaluate ALN-HTT02 in Adult Patients With Huntington's Disease

HDClarity: a Multi-site Cerebrospinal Fluid Collection Initiative to Facilitate Therapeutic Development for Huntington's Disease

This study, HDClarity, aims to gather fluid samples from people with Huntington's disease to find better ways to treat it. By studying blood and spinal fluid, researchers hope to understand the disease better and develop new medicines.

A phase IIa, open label, single centre study to assess the safety, tolerability, pharmacokinetics, pharmacodynamics and preliminary efficacy of orally dosed MBF-015 in Huntington's disease patients

A Phase 2a, Randomized, Placebo-controlled, Dose-Ranging Study to Evaluate the Safety and Efficacy of PTC518 in Subjects with Huntington’s Disease