- enrolling by invitation
Registry of Patients With Hypophosphatasia
This study is gathering information over a long time about people in the UK and other countries who have a rare bone condition called Hypophosphatasia (HPP). It aims to understand how HPP affects people of all ages and how they respond to treatment.
United States · Australia · Austria - recruitingPHASE1, PHASE2
A Study to Assess Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of ALE1 in Healthy Adults and Adults With Hypophosphatasia in Order to Identify Suitable Doses of ALE1
This study is looking into a new medicine called ALE1 for a rare bone condition called Hypophosphatasia (HPP). It will first check if ALE1 is safe in healthy adults, then see how it works in adults with HPP. The aim is to find suitable doses.
New Zealand · United Kingdom