Immune-Mediated Thrombotic Thrombocytopenic Purpura, Thrombotic microangiopathy research hub

An Adaptive Dose Escalation and Expansion Basket Trial to Explore the Safety, Pharmacology, and Clinical Activity of TGD001 in Immune-Mediated Thrombotic Thrombocytopenic Purpura (iTTP) and Other Thrombotic Microangiopathies

This study is testing a new medicine, TGD001, for a rare blood condition called iTTP and similar disorders. It aims to see if the medicine is safe and how it works in the body, as well as if it helps people get better. We're looking at different doses to find the best one.