- recruiting
Understanding the Long-Term Management of Organic Acidemia Patients With CARBAGLU®: A Mixed Methods Approach
This study looks at how a medicine called Carglumic Acid helps people with rare conditions called Methylmalonic Acidemia (MMA) and Propionic Acidemia (PA) over a long time. It gathers information from patient records and talks to patients and their families.
France · Germany · Italy - recruitingPHASE1, PHASE2
An Extension Study to Evaluate the Long-Term Safety and Clinical Activity of mRNA-3705 in Participants Previously Enrolled in Other Clinical Studies of mRNA-3705
This study looks at the long-term safety and effects of a medicine called mRNA-3705 for people with Methylmalonic Acidemia (MMA). It's for those who have already taken part in earlier studies of this same medicine. We want to see how it works and if it's safe over a longer time.
United States · Canada · France