- recruitingPHASE3
KHENERFIN Study: A Trial to Evaluate the Efficacy and Safety of Sonlicromanol in Primary Mitochondrial Diseases
This study, called KHENERFIN, looks at a new medicine called sonlicromanol for people with mitochondrial diseases. It aims to see if the medicine can reduce tiredness and improve physical abilities like balance and strength. Participants will take either the medicine or a dummy pill for a year.
United States · Denmark · France - recruiting
Mitochondrial Donation: An 18 Month Outcome Study.
This study looks at the health and development of babies born using mitochondrial donation, a special IVF technique, up to 18 months old. Researchers want to see if these children develop normally, both physically and mentally, to understand this new treatment better.
United Kingdom