Mitochondrial Diseases research hub

KHENERFIN Study: A Trial to Evaluate the Efficacy and Safety of Sonlicromanol in Primary Mitochondrial Diseases

This study, called KHENERFIN, looks at a new medicine called sonlicromanol for people with mitochondrial diseases. It aims to see if the medicine can reduce tiredness and improve physical abilities like balance and strength. Participants will take either the medicine or a dummy pill for a year.