Neurofibromatosis Type 1 (NF1) Associated Plexiform Neurofibromas (PN) research hub

A Phase 1B, Open-Label Study of Mirdametinib in Infants and Toddlers with Neurofibromatosis Type 1 associated Plexiform Neurofibromas

This study is looking at a new medicine called Mirdametinib for babies and toddlers with a condition called Neurofibromatosis Type 1 (NF1). It aims to check if the medicine is safe and how it affects benign tumours called plexiform neurofibromas.