Niemann-Pick disease research hub

A Long-Term follow-up Study to evaluate safety and tolerability of olipudase alfa in patients who completed the DFI12712 or the LTS13632 Study in France - PTA17397

This study looks at the long-term safety of Xenpozyme for Niemann-Pick disease. It's for people who've already been in previous research studies (DFI12712 or LTS13632). Doctors want to see how well people tolerate the medicine over a long time.