Ornithine Transcarbamylase (OTC) Deficiency research hub

Long Term Follow Up to Evaluate DTX301 in Adults With Late-Onset OTC Deficiency

This study is checking on the long-term safety of a treatment called DTX301 for adults with a condition called OTC deficiency. It's for people who've already taken part in an earlier study of DTX301. Researchers want to see how participants are doing over time.