- recruitingPHASE2, PHASE3
A Study to Evaluate the Effect of Aficamten in Pediatric Patients With Symptomatic Obstructive Hypertrophic Cardiomyopathy (oHCM).
This study is looking into a new medicine called Aficamten for young people aged 12-17 with a heart condition called hypertrophic cardiomyopathy (oHCM). It aims to see if the medicine is safe and effective in improving their symptoms, compared to a dummy medicine.
United States · Canada · Italy - active not recruitingPHASE3
Berotralstat Treatment in Children With Hereditary Angioedema
This study looks at a medicine called berotralstat for children aged 2 to 11 with hereditary angioedema (HAE). Researchers want to find the right dose for children based on their weight, check if it's safe, and see how well it prevents HAE attacks.
Austria · Canada · France - recruiting
Infant and Child European Cryoablation Project ICECaP
This study, called ICECaP, is gathering information about a freezing treatment called cryoablation for children with soft tissue problems. It aims to see how well it works, if it's safe, and what results different hospitals are getting.
United Kingdom