Pelizaeus-Merzbacher Disease research hub

Rocket Study: A Study to Characterize Biomarkers and Disease Progression in Participants With Pelizaeus-Merzbacher Disease

This study, called 'Rocket', is for boys aged 6 months to 17 years with a rare condition called Pelizaeus-Merzbacher Disease (PMD). It aims to better understand how PMD develops and how it affects the body over time, which could help develop new treatments.