- enrolling by invitation
A Self-test Home-use Blood Phenylalanine Monitoring System Under the Brand Name Egoo Phe System Has Been Developed for Measurement of Phenylalanine (Phe) in Individuals Diagnosed With Phenylketonuria (PKU): The Study Purpose is to Evaluate Accuracy and Usability
This study is testing a new home blood testing device for people with Phenylketonuria (PKU). It's called the Egoo Phe System. We want to see how accurate it is compared to current tests and how easy it is for people to use at home.
United Kingdom - active not recruitingPHASE1, PHASE2
AAV Gene Therapy Study for Subjects with PKU
This study is testing a new gene therapy called BMN 307 for Phenylketonuria (PKU). Researchers want to see if it's safe and helps adults with PKU by giving them a single treatment. It’s an early-stage study to understand how well it works.
United States · United Kingdom