Research.Patient.info
Primary Mitochondrial Disease research hub
2 indexed studies · 1 currently recruiting
- recruitingPHASE2
Efficacy of KL1333 in Adult Patients With Primary Mitochondrial Disease
This study is looking into a new medicine, KL1333, for people with primary mitochondrial disease. It aims to see if KL1333 can help reduce tiredness and improve physical abilities, compared to a dummy pill.
United States · Belgium · Denmark - ongoing, recruitingTherapeutic exploratory (Phase II)
A Phase 2a Safety, Tolerability, and Pharmacodynamic Study of OMT-28 in PMD patients with myopathy and/or cardiomyopathy and inflammation (PMD-OPTION)
This study, called PMD-OPTION, is testing a new medicine, OMT-28, for adults with Primary Mitochondrial Disease (PMD) who have muscle or heart problems and inflammation. We want to see if the medicine is safe, how the body handles it, and if it can reduce a specific marker in the blood.
Germany · Italy · Netherlands