- active not recruitingPHASE2, PHASE3
A Phase 2/3 Study to Evaluate the Efficacy and Safety of Tinlarebant in Subjects With Stargardt Disease
This study is looking into a new medicine called Tinlarebant for young people aged 12-20 with an eye condition called Stargardt disease. It aims to see if the medicine is safe, if people can take it without too many problems, and if it helps improve their eyesight or slow the disease.
United States · Japan · United Kingdom - recruiting
An Observational Study in Subjects to Follow the Progression of Stargardt Disease Type 1 (STGD1) Caused by Bi-Allelic Autosomal Recessive Mutations in the ABCA4 Gene
This study looks closely at how Stargardt Disease type 1 (STGD1) changes over time. Researchers want to understand the disease better by watching people who have it. This will help them design better studies in the future to test new treatments for Stargardt.
United States · Germany · United Kingdom