Cerebral Adrenoleukodystrophy (CALD) research hub

Long-term Follow-up of Participants With Cerebral Adrenoleukodystrophy Who Were Treated With Lenti-D Drug Product

This study is following up on children and young men who have a serious brain condition called cerebral adrenoleukodystrophy (CALD). They previously received a special gene therapy called Lenti-D (or eli-cel) in an earlier study. This new study checks on their health over a very long time, up to 15 years.