Research.Patient.info

X-Linked Chronic Granulomatous Disease research hub

1 indexed studies · 1 currently recruiting

recruitingPHASE1, PHASE2
Study of EN-374 Gene Therapy in Participants With X-Linked Chronic Granulomatous Disease
This study is testing a new gene therapy called EN-374 for X-linked Chronic Granulomatous Disease (CGD). It aims to see if the treatment is safe and effective in helping the body fight off serious infections, looking initially at adults and then children.
United States · United Kingdom