X-linked Retinoschisis research hub

ATSN-201 Gene Therapy in RS1-Associated X-linked Retinoschisis

This study is looking at a new gene therapy, ATSN-201, for a rare eye condition called X-linked Retinoschisis (XLRS). It aims to see if the treatment is safe and effective for people aged 6 and over who have XLRS caused by a specific gene problem.