AOC 1001 (del-desiran) clinical trials

Global Study of Del-desiran for the Treatment of DM1

This study is testing a new medicine called del-desiran for Myotonic Dystrophy Type 1 (DM1). It's comparing the new medicine to a dummy treatment (placebo) to see if it's safe and helps people with DM1. Participants will receive infusions over about a year.