Autologous CD34+ cells transduced with WASP lentiviral vector clinical trials

Long Term Safety Follow up of Haematopoietic Stem Cell Gene Therapy for the Wiskott Aldrich Syndrome

This study is a long-term check-up for people who had a special gene therapy for Wiskott-Aldrich Syndrome in earlier trials. It’s to make sure the treatment continues to be safe and helpful over many years.