BMN 349 clinical trials

Study of BMN 349 Single Dose in PiZZ and PiMZ/MASH Adult Participants

This study is testing a new medicine, BMN 349, for adults with a genetic liver and lung condition called Alpha-1 Antitrypsin Deficiency (AATD). Doctors want to see if a single dose of the medicine is safe and well-tolerated. It's a Phase 1 study, the first step in testing new treatments.