DYNE-101 clinical trials

Safety, Tolerability, Pharmacodynamic, Efficacy, and Pharmacokinetic Study of DYNE-101 in Participants With Myotonic Dystrophy Type 1

This study is looking at a new medicine called DYNE-101 for people with Myotonic Dystrophy Type 1 (DM1). We want to check if it's safe, how well people tolerate it, and if it helps with the condition. It involves injections and visits over a long period.