ENTR-601-45 clinical trials

A Study in Participants With Duchenne Muscular Dystrophy Amenable to Exon 45 Skipping to Evaluate the Safety and Efficacy of ENTR-601-45

This study looks at a new medicine, ENTR-601-45, for boys aged 4-20 with Duchenne muscular dystrophy (DMD) where skipping exon 45 is possible. We want to see if it's safe, what side effects it might have, and if it could help. It involves regular clinic visits and infusions.