Evrysdi 0.75 mg/mL powder for oral solution clinical trials

Longitudinal study of clinical outcome measures in adult patients with Spinal Muscular Atrophy (SMA) treated with Risdiplam.

This study looks at how a medicine called Risdiplam (also known as Evrysdi) helps adults with Spinal Muscular Atrophy (SMA) type 2 or 3. Doctors want to see if it improves their daily life and how their bodies are working over two years. It's a big step to understand this treatment better.