- Active not recruitingPHASE3
A Phase III Study of JR-141 in Patients With Mucopolysaccharidosis II (STARLIGHT)
This study is testing a new medicine, JR-141, for people with Mucopolysaccharidosis II (MPS II), also known as Hunter syndrome. It compares JR-141 to an existing treatment, idursulfase, to see if it's safe and works well. This is a large study with many people.
For: Mucopolysaccharidosis IIUnited States · Argentina · Brazil - RecruitingPHASE2, PHASE3
A Study to Determine the Efficacy and Safety of Tividenofusp Alfa (DNL310) vs Idursulfase in Pediatric and Young Adult Participants With Neuronopathic (nMPS II) or Non-Neuronopathic Mucopolysaccharidosis Type II (nnMPS II)
This study is looking at a new medicine called tividenofusp alfa for children and young adults with Mucopolysaccharidosis Type II (MPS II), also known as Hunter syndrome. It compares the new medicine to a standard treatment, idursulfase, to see if it's safe and works well.
For: Mucopolysaccharidosis IIUnited States · Argentina · Australia