ION363 clinical trials

FUSION: A Study to Evaluate the Efficacy, Safety, Pharmacokinetics and Pharmacodynamics of ION363 in Amyotrophic Lateral Sclerosis Participants With Fused in Sarcoma Mutations (FUS-ALS)

This study, called FUSION, is looking at a new medicine called ION363 for people with a specific type of Motor Neurone Disease (MND) called FUS-ALS. It aims to see if ION363 can help with symptoms and survival for those with a particular gene change.