JR-141 clinical trials

A Phase III Study of JR-141 in Patients With Mucopolysaccharidosis II (STARLIGHT)

This study is testing a new medicine, JR-141, for people with Mucopolysaccharidosis II (MPS II), also known as Hunter syndrome. It compares JR-141 to an existing treatment, idursulfase, to see if it's safe and works well. This is a large study with many people.