LNP1265 clinical trials

A Study to Investigate the Safety and Effectiveness of a Coagulation Factor IX Gene Insertion Therapy (REGV131-LNP1265) in Pediatric, Adolescent and Adult Participants With Hemophilia B

This study looks at a new gene therapy called REGV131-LNP1265 for people with haemophilia B. It aims to see if it's safe and helps the body make its own clotting factor, potentially reducing the need for regular treatments.