Migalastat HCl 20 mg clinical trials

A Study of Migalastat in Pediatric Subjects (2 to <12 Yrs) With Fabry Disease and Amenable GLA Variants

This study looks at a medicine called Migalastat for children aged 2 to 11 with Fabry disease. It checks if the medicine is safe, how it works in the body, and if it helps children who have a specific type of Fabry disease.