- AuthorisedPhase I and Phase II (Integrated)- Other
A Phase 1/2, Global, Open-Label, Extension Study to Evaluate the Long-Term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study
This study is an extension of a previous trial for Propionic Acidemia. It aims to see how safe and effective a new medicine, mRNA-3927, is over a longer period. Doctors will look closely at any side effects and how patients are doing.
For: Propionic AcidemiaSpain · Netherlands · France - RecruitingPHASE1, PHASE2
A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study
This study looks at the long-term safety and effects of a treatment called mRNA-3927 for propionic acidemia (a rare condition). It's for people who have already taken part in a previous study of this treatment. Researchers want to see how the treatment works over a longer time.
For: Propionic AcidemiaUnited States · Canada · France - RecruitingPHASE1, PHASE2
Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia
This study is testing a new medicine, mRNA-3927, for Propionic Acidemia (PA). We want to understand if it's safe, how well it works, and find the best dose for people with PA, including children and infants.
For: Propionic AcidemiaUnited States · Canada · France