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N-Acetyl-L-Leucine clinical trials
3 indexed studies · 2 currently recruiting
- RecruitingPHASE3
A Pivotal Study of N-Acetyl-L-Leucine on Niemann-Pick Disease Type C
This study is looking at a new medicine called N-Acetyl-L-Leucine for Niemann-Pick Disease Type C. It compares the new medicine to a dummy treatment (placebo) to see if it's safe and helps people aged 4 and older with this condition.
For: Niemann-Pick Disease, Type CUnited States · Australia · Czechia - Active not recruitingPHASE3
A Pivotal Study of N-Acetyl-L-Leucine on Ataxia-Telangiectasia (A-T)
This study is testing a new medicine, N-Acetyl-L-Leucine, for Ataxia-Telangiectasia (A-T). It aims to see if the medicine is safe, well-tolerated, and effective in improving symptoms, compared to a dummy treatment.
For: Ataxia-Telangiectasia · Ataxia-Telangiectasia (A-T)United States · Germany · Slovakia - Not yet recruitingPHASE3
Pivotal Study of N-acetyl-L-leucine for CACNA1A
This study is looking into a new treatment called N-acetyl-L-leucine for people aged 4 and over with certain genetic conditions like CACNA1A. It aims to see if the treatment is safe, effective, and well-tolerated compared to a dummy pill.
For: CACNA1A · Spinocerebellar Ataxia Type 6 · Episodic Ataxia Type 2United States · Austria · Germany