- Ongoing, recruitingTherapeutic exploratory (Phase II)
A Phase 2, randomised, double-blind, placebo-controlled, 2-way crossover study to evaluate the efficacy, safety, and tolerability of NMD670 in ambulatory adults with Type 3 spinal muscular atrophy
This study is looking at a new medicine called NMD670 for adults with Type 3 spinal muscular atrophy (SMA). It wants to see if NMD670 can help people walk further and feel stronger. Participants will try either NMD670 or a dummy medicine, then switch.
For: Type 3 spinal muscular atrophyNetherlands · Spain · Belgium - Ongoing, recruitingTherapeutic exploratory (Phase II)
A Phase 2a, Randomised, Double-Blind, Placebo-Controlled Study to Evaluate the Efficacy, Safety, and Tolerability of NMD670 over 21 days in Ambulatory Adult Patients with Charcot-Marie-Tooth Disease Type 1 and Type 2
This study is testing a new medicine, NMD670, for people with Charcot-Marie-Tooth disease types 1 and 2. It compares the medicine to a dummy pill to see if it helps people walk further and if it's safe over 21 days. Participants will be adults who can walk.
For: Charcot-Marie-Tooth Disease Type 1 and Type 2Spain · Belgium · France