All treatments
Treatment
Onpattro 2 mg/mL concentrate for solution for infusion. clinical trials
2 indexed studies · 0 currently recruiting
- Ongoing, recruitingTherapeutic confirmatory (Phase III)
A Phase 3, Randomized, Double-blind, Placebo-controlled Multicenter Study to Evaluate the Efficacy and Safety of Patisiran in Patients with Transthyretin Amyloidosis with Cardiomyopathy (ATTR Amyloidosis with Cardiomyopathy)
This study is testing a new medicine, Onpattro, for a heart condition called ATTR amyloidosis. It compares the medicine to a dummy treatment to see if it improves walking ability and overall heart health in adults.
For: Transthyretin Amyloidosis with Cardiomyopathy (ATTR Amyloidosis with Cardiomyopathy)Denmark · Belgium · Italy - Ongoing, recruitingTherapeutic confirmatory (Phase III)
HELIOS-A: A Phase 3 Global, Randomized, Open-label Study to Evaluate the Efficacy and Safety of ALN-TTRSC02 in Patients With Hereditary Transthyretin Amyloidosis (hATTR Amyloidosis)
This study is testing a new medicine, Amvuttra, for a rare inherited condition called hereditary transthyretin amyloidosis (hATTR amyloidosis). It aims to see if Amvuttra is safe and helps improve symptoms compared to standard treatments.
For: Hereditary Transthyretin AmyloidosisNetherlands · Belgium · Cyprus