PRX-102 1 mg/kg every two weeks clinical trials

A Study to Learn About the Safety and Effects of the Study Drug PRX-102 in Children and Adolescents With Fabry Disease

This study is testing a new medicine, PRX-102, for children and teenagers aged 2-17 with Fabry disease. We want to see how safe it is and how well it helps with symptoms like pain and heart or kidney problems.