RO7034067 clinical trials

An Open-Label Study to Investigate the Safety, Tolerability, and Pharmacokinetics/Pharmacodynamics of Risdiplam (RO7034067) in Adult and Pediatric patients with Spinal Muscular Atrophy

This study is looking at a new medicine called Risdiplam for people with Spinal Muscular Atrophy (SMA). We want to understand how safe it is, if it causes side effects, and how the body handles the medicine. It's for both adults and children.