- RecruitingPHASE3
Study to Evaluate Sepofarsen in Subjects With Leber Congenital Amaurosis (LCA) Type 10 (HYPERION)
This study is testing a new medicine called sepofarsen for a rare eye condition called Leber Congenital Amaurosis Type 10 (LCA10). It aims to see if sepofarsen can improve vision safely in people with this condition.
For: Leber Congenital Amaurosis 10 · Blindness · Leber Congenital AmaurosisUnited States · Belgium · Brazil - Active not recruitingPHASE2, PHASE3
A Study to Evaluate Efficacy, Safety, Tolerability and Exposure After a Repeat-dose of Sepofarsen (QR-110) in LCA10 (ILLUMINATE)
This study looks at a new treatment called sepofarsen for a rare eye condition called Leber Congenital Amaurosis 10 (LCA10), which causes blindness. We want to see if it helps improve sight, how safe it is, and how well people tolerate it.
For: Leber Congenital Amaurosis 10 · Blindness · Leber Congenital AmaurosisUnited States · Belgium · Brazil