Treatment

SHP611 clinical trials

1 indexed studies · 0 currently recruiting

Active not recruitingPHASE2
A Study of Intrathecal SHP611 in Children With Metachromatic Leukodystrophy
This study is looking at a new medicine called SHP611 for children with Metachromatic Leukodystrophy (MLD). Doctors want to see if SHP611, given into the spinal fluid, can help children keep their ability to move around for longer. It also looks at how it affects speech and if it's safe.
For: Metachromatic Leukodystrophy (MLD)
United States · Argentina · Belgium