Treatment

SPK-3006 clinical trials

1 indexed studies · 0 currently recruiting

Active not recruitingPHASE1, PHASE2
A Gene Transfer Study for Late-Onset Pompe Disease (RESOLUTE)
This study is testing a new medicine called SPK-3006 for adults with late-onset Pompe disease. It aims to see if it's safe and helps improve the condition. Participants will receive one dose of the new medicine and will be carefully checked.
For: Pompe Disease · Pompe Disease (Late-onset) · Glycogen Storage Disease Type 2
United States · Canada · Denmark