SRP-9003 clinical trials

A Trial to Learn More About an Experimental Gene Therapy Called Bidridistrogene Xeboparvovec (SRP-9003) as a Possible Treatment for Limb Girdle Muscular Dystrophy 2E/R4

This study is testing an experimental gene therapy, SRP-9003, for Limb-girdle Muscular Dystrophy type 2E/R4 (LGMD2E/R4). It aims to see how a single dose affects a specific gene in people who can walk and those who can't.