TSHA-102 clinical trials

Safety and Efficacy of TSHA-102 in Pediatric Females With Rett Syndrome (REVEAL Pediatric Study)

This study is looking at a new gene therapy called TSHA-102 for girls aged 5-8 with Rett Syndrome. It aims to see if the treatment is safe and how well it works to help with their condition. It's an early-stage study to learn more about this potential new medicine.