Latest studies
- RecruitingPHASE3
Acoramidis Transthyretin Amyloidosis Prevention Trial in the Young (ACT-EARLY) Study in Asymptomatic Carriers of a Pathogenic TTR Variant
This study looks at a new drug, acoramidis, for people who have a faulty gene that can cause a condition called ATTR. It aims to see if the drug can stop or slow down the disease from developing in people who don't yet have symptoms.
AmyloidosisAmyloid CardiomyopathyTransthyretin AmyloidosisCardiomyopathiesMartinique - Recruiting
Global Patient Registry to Monitor Long-term Safety and Effectiveness of Increlex® in Children and Adolescents With Severe Primary Insulin-like Growth Factor-1 Deficiency (SPIGFD).
This study is a registry tracking the long-term safety and effectiveness of Increlex® in children and teenagers with a specific growth condition (SPIGFD). It involves collecting information from patients already using the medication to understand its real-world impact.
IGF1 DeficiencyMartinique - RecruitingNA
Prevention Of Sudden Cardiac Death After Myocardial Infarction by Defibrillator Implantation
This study looks at whether a small device, called a defibrillator, is still the best way to prevent sudden death in people who have had a heart attack and have a weakened heart. We want to see if modern medicines alone are just as good.
Sudden Cardiac DeathMyocardial InfarctionMartinique